CAMBRIDGE, Mass. and PARIS, Aug. 01, 2018 (GLOBE NEWSWIRE) -- Lysogene (FR0013233475 – LYS), a pioneering biopharmaceutical company specializing in gene therapy targeting central nervous system (CNS) diseases, today announced upcoming oral and poster presentations at the 2018 International MPS Symposium being held August 2-5, 2018, in San Diego.
Design and rationale of the LYS-SAF302 gene therapy study in mucopolysaccharidosis type IIIA (MPS IIIA) children Presenter: Karen Aiach, Founder and Chief Executive Officer at Lysogene, France. Thursday, August 2, 2018 Time: 5.30 - 7 PM PDT
Design, baseline characteristics, and 12-18 months follow-up from the mucopolysaccharidosis type IIIA (MPS IIIA) natural history studyPresenter: Frits Wijburg, MD, Principal Investigator, Academic Medical Center Genetic Metabolic Disorders, Netherlands. Thursday, August 2, 2018 Time: 5.30 - 7 PM PDT
Capturing the MPS IIIA patient and family voice in orphan drug development to appreciate what is important in managing the disease and improving quality of life Presenter: Samantha Parker, Chief Patient Access Officer at Lysogene, France. Friday, August 3, 2018 Time: 5.30 - 7 PM PDT
AAV gene therapy LYS-SAF302 demonstrates widespread sulfatase distribution in primate brain and correction of disease pathology in MPSIIIA mice Presenter: Ralph Laufer, Ph.D., Chief Scientific Officer at Lysogene Date: Saturday, August 4, 2018 Time: 1.15 PM PDT
The 15th International MPS and related diseases Symposium 2018 is hosted in San Diego, CA, US. The symposium, features scientific and family focused tracks to meet the needs of all attendees. It is an opportunity for the MPS and related diseases community to share and exchange new information, learn about new breakthroughs in science and medicine, and develop strategies to keep the MPS community moving forward.
Lysogene is a gene therapy company focused on the treatment of orphan diseases of the central nervous system (CNS). The company has built a unique capability to enable a safe and effective delivery of gene therapies to the CNS to treat lysosomal diseases and other genetic disorders of the CNS. A pivotal clinical trial in MPS IIIA and a phase 1-2 clinical trial in GM1 Gangliosidosis are in preparation, while we are currently collaborating with a major partner to define the strategy of development for the treatment of Fragile X syndrome, a genetic disease related to autism. www.lysogene.com
Julie Coulot / Emmanuel HuynhNewCaplysogene@newcap.eu+ 33 1 44 71 94 95
Forward looking statement
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